Februar 28, 2023
Rare disease day: Highlighting the therapeutic potential of cell and gene therapies

Rare is many: 300 million people worldwide live with a rare disease.

Let’s raise awareness for the many, their families and friends & work together to effectively translate high value research findings into faster diagnostic procedures, support measures, and first-time-therapies.


Thank you Tagesspiegel, Deutschlandfunk and NDR Info for highlighting „the many rare“ and for giving us the opportunity to inform about our mission of developing effective advanced therapies for muscle disorders.